exagamglogene autotemcel
exagamglogene autotemcel
Autologous CD34+ cells isolated from mobilised peripheral blood by positive selection, modified by CRISPR/Cas9 (clustered regularly interspaced short palindromic repeats/CRISPR-associated protein 9) mediated gene editing consisting of a guide RNA (gRNA)
autologous cd34+ cells isolated from mobilised peripheral blood by positive selection, modified by crispr/cas9 (clustered regularly interspaced short palindromic repeats/crispr-associated protein 9) mediated gene editing consisting of a guide rna (grna)