atidarsagene autotemcel
atidarsagene autotemcel
Autologous CD34+ cell enriched population that contains haematopoietic stem and progenitor cells (HSPC) transduced ex vivo using a lentiviral vector encoding the human arylsulfatase A (ARSA) gene
autologous cd34+ cell enriched population that contains haematopoietic stem and progenitor cells (hspc) transduced ex vivo using a lentiviral vector encoding the human arylsulfatase a (arsa) gene